Cell and gene therapy companies list. Jul 26, 2022 · [Check out our updated list featuring 100 cell and gene therapy companies. These include reliable sources of GMP compatible starting material, clinical trial support for complex cell therapy workflows, and hospitals capable of administering advanced therapies. BridgeBio is a US-based biotechnology company that develops drugs to treat several genetic diseases and cancer. Cell therapy products include immunotherapies, cancer vaccines, and other types of both autologous and allogeneic cells designed to treat different conditions. Catalent is a leading global CDMO, trusted by pharma, biotech and self-care companies to accelerate the development, manufacturing and delivery of products that improve lives. Mar 2, 2026 · Shares of uniQure plummeted more than 40% in premarket trading Monday after the company confirmed the FDA has rejected its current data package for AMT-130, a highly anticipated gene therapy for Gene therapy may be classified into two types by the type of cell it affects: somatic cell and germline gene therapy. Feb 27, 2026 · The Managing Director, Health System Solutions – Cell & Gene Therapy (CGT) is responsible for the execution and operational leadership of Cencora’s consulting solutions for hospitals and health systems in the CGT space. 7 hours ago · The report provides a comprehensive analysis of the global Cell and Gene Therapy Manufacturing Market, covering revenue forecasts from 2024 to 2032. Intellia Therapeutics was founded in 2014 and is headquartered in Cambridge, Massachusetts, US. , Biogen Inc. Allogene Therapeutics has Unveiled the Potential of Allogeneic Cell Products as Off-the-Shelf Therapeutics for Hematological and Oncological Malignancies. BridgeBio is Rigorously Pioneering the Development of Gene Therapies for Debilitating Diseases. Engineered T cells are expanded in tissue culture 5. Iovance Biotherapeutics is a US-based company that specializes in the development and discovery of novel tumor infiltrating lymphocyte (TIL) therapies. ] Our list of prominent cell and gene therapy companies includes top-tier Big Pharma companies as well as smaller privately-held companies. CRISPR-based differentiated technologies are the cornerstones at Intellia Therapeutics for the Investigation of Patient-Focused Treatment. This is designed to induce partial epigenetic reprogramming to modify the epigenome of cells. Explore the top cell therapy companies, including Kite Pharma and Juventas, revolutionizing cancer treatment and patient care worldwide. 6 days ago · Another emerging trend in the Cancer Biologics Market Outlook involves the increasing development of CAR-T cell therapy and gene-modified biologic treatments. Iovance Biotechnology’s TIL Therapy Manufacturing Capabilities have yielded in the Treatment of over 600 Patients, worldwide. . , JCR Pharmaceuticals Co. , CORESTEM Inc. Without these components in place The FDA approved the first cell-based gene therapies, Casgevy and Lyfgenia, for the treatment of sickle cell disease in patients 12 years and older. D. Jan 14, 2025 · The top companies in cell and gene therapy are Alnylam Pharmaceuticals Inc. , Helixmith Co. 1 day ago · How can smaller gene and cell therapy companies compete for top-tier executive talent with larger biopharmas? Smaller companies often leverage their innovative science, unique culture, potential for greater impact, and significant equity upside. Nov 28, 2024 · Biopharma companies are actively exploring these therapies across multiple indications to address healthcare gaps in rare and chronic diseases. Approximately 27% of advanced cancer therapy research programs involve cell-based therapies, targeting blood cancers and solid tumors. In somatic cell gene therapy (SCGT), the therapeutic genes are transferred into any cell other than a gamete, germ cell, gametocyte, or undifferentiated stem cell. , Dendreon Pharmaceuticals LLC. Ltd. , who called the decision “truly evil” in an interview with The New York Times. T cells are isolated from a patient's blood 2. Revenues for 5 days ago · The FDA’s rejection of uniQure’s gene therapy drew the ire of former senior agency official Janet Woodcock, M. Jan 19, 2026 · These startups develop therapies that manipulate gene expression or altere the biological properties of living 5 days ago · Cell and gene therapy companies rely on several critical pieces of infrastructure to move therapies from development to clinical trials and ultimately to patient treatment. View the list and locations of 440 biotechnology companies engaged in Cell and Gene Therapy work. CELL AND GENE THERAPY Intellia’s CRISPR Gene Therapy Free To Move Forward After FDA Fully Lifts Hold REGENXBIO’s Hunter Rejection Hinged on Inadequate Controls, Surrogate Endpoint UniQure Eyes Phase 3 for Huntington’s Gene Therapy Despite Makary’s Apparent Criticism Sep 10, 2024 · Novartis is also developing a cell and gene therapy technology platform that includes adeno-associated virus-based therapy, CAR T-cell therapy and gene therapy based on CRISPR. , Amgen Inc. Engineered T cells are now specific to a desired target antigen 4. 4 days ago · The company’s lead program is a gene therapy called ER-100, which allows for the expression of three transcription factors known as OCT4, SOX2, and KLF4. , Novartis AG, and Pfizer Inc. A new gene encoding a chimeric antigen receptor is incorporated into the T cells 3. With advanced technologies, deep expertise and a worldwide network, we partner with innovators to transform bold ideas into life-changing therapies and self-care solutions. , Kolon TissueGene Inc. This role focuses on delivering client engagements, enhancing service offerings, and managing the financial performance of the portfolio, including revenue and gross profit CAR T cell Chimeric antigen receptor T cell production and infusion: 1. PharmaShots presents a concise report on the top 20 cell and gene therapy companies of 2024. sdxj tnig xfeirnj mjqkn rwew hwjakc eyzhsm ipbwk phrajb xpbaj